Born in Morristown, N.J., with virtually no immune system, Cora was diagnosed with severe combined immunodeficiency, a rare ...

Oliver Chu was born with a rare genetic condition called Hunter syndrome that impacts physical and mental development. The ...

Oliver has an inherited condition called Hunter syndrome, which causes progressive damage to the body and brain.

Fred Hutch bioengineer Dr. Matthias Stephan is working to develop a special foam that could help make gene therapy for blood ...

Cell and gene therapies represent a transformative frontier in modern medicine, offering potential cures for previously untreatable conditions. However, securing intellectual property (IP) protection ...

This academic-industry partnership reflects the need for a multidisciplinary approach to innovation in cell and gene therapy manufacturing.

The CRISPR Cas9 gene editing tool — the genetic scissors that won the 2020 Nobel Prize in Chemistry — is essentially based on ...

Yas Clinic – Khalifa City, in collaboration with the Abu Dhabi Stem Cells Centre (ADSCC) and Vertex Pharmaceuticals, has announced a landmark partnership to introduce gene therapy in the UAE for the ...

Genprex, Inc. ("Genprex" or the "Company") (NASDAQ: GNPX), a clinical-stage gene therapy company focused on developing ...

The Minister noted that with the development and transfer of India's first indigenous CRISPR-based gene therapy, the nation ...

Mixed headlines have plagued the cell and gene therapy space of late. We believe that a renewed case of optimism is not only ...

Through substantial leadership turnover and workforce cuts, the FDA has continued to support the advanced therapy sector, ...