Under the agreement, participating states will receive “discounts and rebates” from the drugmakers if the treatments don’t ...

When it was announced in 2023 that the world’s first Crispr-based gene-editing therapy had been approved in the UK there was ...

Medicaid is doing a novel payment system for the new, promising and expensive sickle cell treatment. It may become a model ...

A year ago, NBC News joined Wedam Minyila as he began undergoing a groundbreaking treatment for sickle cell disease. The process has included having his stem cells removed for a revolutionary gene ...

NHS Scotland has approved a one-time CRISPR gene therapy for severe sickle cell disease, offering durable reduction in vaso-occlusive crises for eligible patients.

After 35 years of consistent pain, Allan Byamukama became one of the few individuals in the world cured of sickle cell ...

Starting in his early teens, Deshawn "DJ" Chow wasn't sure he'd ever be able to live a normal life. Crushing pain episodes brought on by his sickle cell disease were getting progressively worse. "It's ...

LOS ANGELES (KABC) -- It's been more than a month since the FDA approved two milestone gene-editing treatments for sickle cell disease, but lining up patients for these therapies will be a challenge ...

Evelyn Quartey carries the sickle cell trait, as did her ex-husband and first son, Emmanuel, who passed away from Sickle Cell Disease in 2009 at 7. Her younger son Gerald had been diagnosed with the ...

The U.S. Food and Drug Administration (FDA) on Friday announced that it has approved Casgevy, the first CRISPR gene-editing therapy for sickle cell disease, paving the way for thousands of patients in ...

The first study assessing the real-world commercial roll-out of gene therapies for sickle cell disease and beta thalassemia offers lessons learned to inform best practices as manufacturers and medical ...

A new gene therapy for people who can have a stem cell transplant but do not have a suitable donor has been approved.