News

Another gene therapy death of a Duchenne patient has some parents and doctors criticizing the FDA's actions, even as other ...
Muscular dystrophy refers to a group of rare, genetic, progressive diseases that primarily affect the body’s muscles, causing ...
U.S. FDA grants Orphan Drug Designation to Deramiocel for the treatment of Becker Muscular Dystrophy, broadening Capricor’s ...
The boys live in Reed City with their mother Tabatha; father Michael, who is the Osceola County Road Commission manager and ...
Panelists discuss how data from MDA 2025 demonstrate that delandistrogene moxeparvovec (gene therapy for DMD) shows ...
Roche (SIX:ROG) shares dropped 2% on Monday after the company paused dosing of its gene therapy Elevidys in non-ambulatory ...
What Happened? Shares of biotech company Sarepta Therapeutics (NASDAQ:SRPT) fell 44.4% in the afternoon session after the ...
Panelists discuss how recent advancements in muscular dystrophy treatment have evolved toward truly disease-modifying ...