Cardiovascular medicine is undergoing transformative change as gene therapy emerges as a promising approach to address heart failure and cardiac ...
ACM impedes the heart from pumping blood to the rest of the body, and is a leading cause of sudden cardiac death in young ...
UniQure had planned to seek accelerated approval for AMT-130 early 2026, but then said its plans were stalled after ...
U.S. drugmaker Eli Lilly signed an agreement worth up to $1.12 billion with Seamless Therapeutics, the Germany-based startup ...
Researchers developed a topical gene therapy that corrects disease-causing mutations in human skin models using lipid ...
Gene-editing tools like CRISPR have unlocked new treatments for previously uncurable diseases. Now, researchers at the ...
Gene-editing tools like CRISPR have unlocked new treatments for previously uncurable diseases. Now, researchers at the ...
CRISPR therapy STX-1150 could replace daily cholesterol pills with a single dose, reducing LDL by 50% for 18+ months using ...
Sarepta Therapeutics' gene ‌therapy for Duchenne muscular dystrophy slowed disease progression and showed sustained benefit ...
Inaugural event takes place from 9–10 March at Hinxton Hall in Cambridge, UKProgramme spans neurological disorders, sensory ...
Chinese scientist He Jiankui wants to end Alzheimer’s and thinks Silicon Valley is conducting a “Nazi eugenic experiment.” ...